Rare & Orphan Disease Clinical Development Expertise

Veristat is passionate about helping clients accelerate their rare disease therapies for unmet medical needs through the clinical development process. With over 350 million rare disease sufferers worldwide today, the urgency for more treatments is paramount. Veristat is proud to have worked on over 300 rare disease treatments so far!

Rare Disease Trials Require Dedicated Expertise

As there are at least 7,000 rare diseases affecting patients today, each type of which exhibits very unique and diverse symptomatology, what makes Veristat unique is our ability to problem solve, develop creative solutions and apply our scientific knowledge and expertise to each new therapy.

Our teams are passionate and work tirelessly to learn and become experts in every unique and rare disease indication we work in.   To date, we've worked on hundreds of clinical projects and have prepared over 35 regulatory submissions for rare disease products.


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Explore  Our Recent Rare Disease Experience

Below is a sampling of our diverse rare disease clinical trial and regulatory submission experience.   Contact us to learn more about specific experience.

  • Autoimmune Diseases such as Idiopathic Thrombocytopenia Purpura (ITP) or Raynaud’s Phenomenon
  • Infectious Diseases such as Ebola or West Nile Virus
  • Cardiovascular Disease such as Homozygous Familial Hypercholesterolemia (HoFH)
  • CNS/Neurological Disorders such as Alzheimer's Disease or Multiple Sclerosis (MS)
  • Genetic Disorders such as Cystic Fibrosis or Thalasseemia
  • Hematologic Malignancies such as Multiple Myeloma or Myeloid Leukemia 
  • Solid Tumor Cancers such as Non-Small Cell Lung Cancer (NSCLC) or Pancreatic Cancer

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We will help you pioneer and revolutionize therapies for patients with limited or no other treatment options. Whether you are looking to prevent, diagnose, cure or improve quality or length of life for rare disease sufferers, look no further than Veristat.  

Our teams will partner to guide you through the design and management of your clinical development project or program. And, we’ll help you plan and navigate the regulatory submission process. Contact us to learn more about our experiences and how we can apply our experience and knowledge to your study.  

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