Endocrine and Metabolic Disease Clinical Development Expertise

Overcoming complexities to bring more metabolic disease treatments to market successfully

Metabolic diseases are a rising therapy area focus for clinical research due to high demand for novel therapies that are challenged with proving safety and efficacy. The development process is complicated and full of unknowns, and even the best metabolic therapeutic might not make it to the patients that need it, not because it does not work but because the design, data collection, and analysis were not done right. 

At Veristat, we have assembled an extraordinary team of scientific-minded experts who have mastered the complexities of running metabolic disease trials.   Our team has supported >180 clinical trials for endocrine/metabolic disorders and the preparation of 15 marketing applications - 13 of which have been approved so far! 

Success with Lifestyle, Genetic, and Rare Metabolic Therapies

We strive to advance your novel metabolic therapies from Phase I-III clinical development to market with confidence.  

Our experienced teams are poised to plan and implement these efforts quickly, providing:     

Proven Expertise for Success

> 180

Endocrine/Metabolic Trials



are Rare Disorders

Veristat_icon_gene therapy

> 70%

are Genetic Disorders

Explore Our Endocrine Experience

Get the right strategic consultation, clinical program implentation, regulatory approval registration, and post-marketing support for endocrine and metabolic therapies based upon our extensive first-hand knowlege.   

Breadth of Therapy Indications
Gaucher Disease
Adrenoleukodystrophy (ALD) and Thalassemia
Generalized Lipodystrophy
Lysosomal Acid Lipase (LAL) Deficiency
Alpha-mannosidosis (AM)
Gout (Hyperuricemia)
Maroteaux-Lamy Syndrome
Growth Hormone Deficiencies/Abnormalities
Molybdenum Cofactor Deficiency
Bardet-Biedl Syndrome and Alstrom Syndrome
Hereditary ATTR (hATTR) Amyloidosis
Mucopolysaccharidosis type IIIB
Cerebral Adrenoleukodystrophy
Multiple Lysosomal Storage Disorders
Chronic Pancreatitis
Homozygous Familial Hypercholesterolemia (HoFH)
Non-Alcoholic Steatohepatitis (NASH)
Congenital Adrenal Hyperplasia
Pharmacodynamic Markers
POMC deficiency
Fabry Disease
Hypoleptinemic Dysmetabolic Disorder
Pompe Disease
Familial Amyloid Polyneuropathy
Pyruviate Kinase Deficiency
Familial Chylomicronemia Syndrome (FCS)
Immunoglobulin A (IgA) Nephropathy
Vasomotor symptoms (VMS)


Learn More with These Resources

Case Study
Preparing Data for a Marketing Authorization Application ...

Read the case study to learn how we helped a biotech prepare the MAA submission for a recently acquired product. Our creative approach included utilizing one DB for ...

Conference Presentation
Turning Sponsor/CRO Relationships into Partnerships for ...

Get the presentation that was given at the Evolution Summit Fall 2019. Veristat and thier client Ascendis Pharma share thier thoughts on how to truly work as a ...

Case Study
Running Successful Clinical Programs with an External ...

A biopharmaceutical firm specializing in rare and ultra-rare disease research started working with Veristat over 7 years ago.

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