Endocrine and Metabolic Disease Clinical Development Expertise

Overcoming complexities to bring more metabolic disease treatments to market successfully

Metabolic diseases are a rising therapy area focus for clinical research due to high demand for novel therapies that are challenged with proving safety and efficacy. The development process is complicated and full of unknowns, and even the best metabolic therapeutic might not make it to the patients that need it, not because it does not work but because the design, data collection, and analysis were not done right. 

At Veristat, we have assembled an extraordinary team of scientific-minded experts who have mastered the complexities of running metabolic disease trials.   Our team has supported >180 clinical trials for endocrine/metabolic disorders and the preparation of 15 marketing applications - 13 of which have been approved so far! 

Success with Lifestyle, Genetic, and Rare Metabolic Therapies

We strive to advance your novel metabolic therapies from Phase I-III clinical development to market with confidence.  

Our experienced teams are poised to plan and implement these efforts quickly, providing:     

Proven Expertise for Success
Veristat_icon_endocrinology-metabolic-216

> 180

Endocrine/Metabolic Trials


Veristat_icon_rare-disease-216

80%

are Rare Disorders


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> 70%

are Genetic Disorders



Explore Our Endocrine Experience

Get the right strategic consultation, clinical program implentation, regulatory approval registration, and post-marketing support for endocrine and metabolic therapies based upon our extensive first-hand knowlege.   

Breadth of Therapy Indications
  
Achondropasia
  
Gaucher Disease
  
Lipodystrophy
  
Adrenoleukodystrophy (ALD) and Thalassemia
  
Generalized Lipodystrophy
  
Lysosomal Acid Lipase (LAL) Deficiency
  
Alpha-mannosidosis (AM)
  
Gout (Hyperuricemia)
  
Maroteaux-Lamy Syndrome
  
Anorexia
  
Growth Hormone Deficiencies/Abnormalities
  
Molybdenum Cofactor Deficiency
  
Bardet-Biedl Syndrome and Alstrom Syndrome
  
Hereditary ATTR (hATTR) Amyloidosis
  
Mucopolysaccharidosis type IIIB
  
Cerebral Adrenoleukodystrophy
  
Homocystinuria
  
Multiple Lysosomal Storage Disorders
  
Chronic Pancreatitis
  
Homozygous Familial Hypercholesterolemia (HoFH)
  
Non-Alcoholic Steatohepatitis (NASH)
  
Congenital Adrenal Hyperplasia
  
Hypercholesterolemia
  
Obesity
  
Diabetes
  
Hyperoxaluria
  
Pharmacodynamic Markers
  
Dyslipidemia
  
Hypertriglyceridemia
  
POMC deficiency
  
Fabry Disease
  
Hypoleptinemic Dysmetabolic Disorder
  
Pompe Disease
  
Familial Amyloid Polyneuropathy
  
Hypoparathyroidism
  
Pyruviate Kinase Deficiency
  
Familial Chylomicronemia Syndrome (FCS)
  
Immunoglobulin A (IgA) Nephropathy
  
Vasomotor symptoms (VMS)

 

Learn More with These Resources

Case Study
Preparing Data for a Marketing Authorization Application ...

Read the case study to learn how we helped a biotech prepare the MAA submission for a recently acquired product. Our creative approach included utilizing one DB for ...

Conference Presentation
Turning Sponsor/CRO Relationships into Partnerships for ...

Get the presentation that was given at the Evolution Summit Fall 2019. Veristat and thier client Ascendis Pharma share thier thoughts on how to truly work as a ...

Case Study
Running Successful Clinical Programs with an External ...

A biopharmaceutical firm specializing in rare and ultra-rare disease research started working with Veristat over 7 years ago.

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